Weboligonucleotide targeting glycogen synthase 1 pre‑mRNA (also known as ION283) for the treatment of progressive myoclonic epilepsy type 2 (Lafora disease). What is progressive myoclonic epilepsy type 2 (Lafora disease)? Lafora disease is an inherited brain disease marked by epileptic seizures (fits) and worsening intellectual function. Webregistratore vocale spia batteria lunga durata Login with LinkedIn. Register; san giorgio acilia orario messe; pronostici marcatori oggi champions
Public summary of opinion on orphan designation
WebFor the biopharma industry investment, business development and competitive intelligence professionals who require information to support financing, partnering and licensing … Web11 feb. 2024 · ION283 is a drug that is expected to prevent new Lafora body formation and halt the progression of Lafora disease. We need to get this drug into clinical trials. Such a trial is estimated to cost $10,000,000. The drug and all the scientific data backing it belongs to Ionis Pharmaceuticals. on-nara bps system
Ionis
Web30 sep. 2024 · ION373 is one of several Ionis-owned investigational medicines designed to treat neurological diseases. Others include ION716 (Prion disease), ION283 (Lafora … WebION283 Lafora disease ION373 Alexander disease R IONIS-AR-2.5 Rx * Prostate Cancer ION929 Cancer ION251 Multiple myeloma ION674* Lymphomas PULMONARY & ALLERGY IONIS-ENAC-2.5 Rx Cystic fibrosis IONIS-PKK-L Rx Hereditary angioedema ION663 Pulmonary disease HEME IONIS -TMPRSS6 L Rx bthalassemia *Licensed to … WebFCA registered and authorised © 2024 DRUGANALYST LTD Cancel Save Save onna richburg